| Title: |
Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series |
| Authors: |
Shneider, Neil A a, *; Harms, Matthew B a; Korobeynikov, Vlad A a; Rifai, Olivia M a; Hoover, Benjamin N a; Harrington, Elizabeth A a; Aziz-Zaman, Sonya a; Singleton, Jessica a; Jamil, Arish a; Madan, Vikram R a; Lee, Ikjae a; Andrews, Jinsy A a; Smiley, Richard M a; Alam, Mahabub M a; Black, Lauren E b; Shin, Minwook c; Watts, Jonathan K d; Walk, David e; Newman, Daniel f; Pascuzzi, Robert M g; Weber, Markus h; Neuwirth, Christoph h; Da Cruz, Sandrine i; Soriano, Armand j; Lane, Roger j; Henry, Scott j; Mathews, Joel j; Jafar-Nejad, Paymaan j; Norris, Dan j; Rigo, Frank j; Brown, Robert H j; Miller, Stephan j; Crean, Rebecca j; Bennett, C Frank j |
| Source: |
In The Lancet 7-13 June 2025 405(10494):2075-2086 |
| Database: |
ScienceDirect |