SMA – THERAPY: P.261 Long-term follow-up of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1 (SMA1)
| Title: | SMA – THERAPY: P.261 Long-term follow-up of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1 (SMA1) |
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| Authors: | Mendell, J. 1; Shell, R. 1; Lehman, K. 1; McColly, M. 1; Lowes, L. 1; Alfano, L. 1; Miller, N. 1; Iammarino, M. 1; Church, K. 1; Ogrinc, F. 2; Ouyang, H. 2; Kernbauer, E. 2; Joshi, S. 2; Sproule, D. 2; Meriggioli, M. 2; Feltner, D. 2; Al-Zaidy, S. 1 |
| Source: | In Neuromuscular Disorders October 2020 30 Supplement 1:S122-S123 |
| Database: | ScienceDirect |