| Title: |
Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic |
| Authors: |
Logan, Todd; Simon, Matthew J.; Rana, Anil; Cherf, Gerald M.; Srivastava, Ankita; Davis, Sonnet S.; Yoon Low, Ray Lieh; Chiu, Chi-Lu; Fang, Meng; Huang, Fen; Bhalla, Akhil; Llapashtica, Ceyda; Prorok, Rachel; Pizzo, Michelle E.; Calvert, Meredith E.K.; Sun, Elizabeth W.; Hsiao-Nakamoto, Jennifer; Rajendra, Yashas; Lexa, Katrina W.; Srivastava, Devendra B.; van Lengerich, Bettina; Wang, Junhua; Robles-Colmenares, Yaneth; Kim, Do Jin; Duque, Joseph; Lenser, Melina; Earr, Timothy K.; Nguyen, Hoang; Chau, Roni; Tsogtbaatar, Buyankhishig; Ravi, Ritesh; Skuja, Lukas L.; Solanoy, Hilda; Rosen, Howard J.; Boeve, Bradley F.; Boxer, Adam L.; Heuer, Hilary W.; Dennis, Mark S.; Kariolis, Mihalis S.; Monroe, Kathryn M.; Przybyla, Laralynne; Sanchez, Pascal E.; Meisner, Rene; Diaz, Dolores; Henne, Kirk R.; Watts, Ryan J.; Henry, Anastasia G.; Gunasekaran, Kannan; Astarita, Giuseppe; Suh, Jung H. |
| Source: |
Cell ; volume 187, issue 6, page 1565-1566 ; ISSN 0092-8674 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2024 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/j.cell.2024.02.015 |
| Availability: |
https://doi.org/10.1016/j.cell.2024.02.015; https://api.elsevier.com/content/article/PII:S0092867424001818?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S0092867424001818?httpAccept=text/plain |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ ; https://www.elsevier.com/legal/tdmrep-license ; http://www.elsevier.com/open-access/userlicense/1.0/ ; https://doi.org/10.15223/policy-017 ; https://doi.org/10.15223/policy-037 ; https://doi.org/10.15223/policy-012 ; https://doi.org/10.15223/policy-029 ; https://doi.org/10.15223/policy-004 |
| Accession Number: |
edsbas.1092E798 |
| Database: |
BASE |