| Title: |
Long-term therapeutic efficacy of intravenous AAV-mediated hamartin replacement in mouse model of tuberous sclerosis type 1 |
| Authors: |
Cheah, Pike See; Prabhakar, Shilpa; Zhang, Xuan; Zinter, Max; Gianatasio, Maria; Bronson, Roderick; Kwiatkowski, David; Stemmer-Rachamimov, Anat; Maguire, Casey; Sena-Esteves, Miguel; Tannous, Bakhos; Breakefield, Xandra |
| Source: |
IBRO Reports ; volume 6, page S504 ; ISSN 2451-8301 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2019 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/j.ibror.2019.07.1575 |
| Availability: |
http://dx.doi.org/10.1016/j.ibror.2019.07.1575; https://api.elsevier.com/content/article/PII:S2451830119316279?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S2451830119316279?httpAccept=text/plain |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ ; http://creativecommons.org/licenses/by-nc-nd/4.0/ |
| Accession Number: |
edsbas.596FC488 |
| Database: |
BASE |