| Title: |
Efficacity and safety of CFTR modulators in patients with interstitial lung disease caused by ABCA3 transporter deficiency |
| Authors: |
Le Brun, Mathilde; Nathan, Nadia; Legendre, Marie; Frija-Masson, Justine; Onanga, Mwetty; Dupin, Clairelyne; Morer, Lise; Debray, Marie-Pierre; Fajac, Isabelle; Burgel, Pierre-Régis; Crestani, Bruno; Borie, Raphaël |
| Contributors: |
AP-HP - Hôpital Bichat - Claude Bernard Paris; Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP); CHU Trousseau APHP; Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU); Maladies génétiques d'expression pédiatrique (U933); Institut National de la Santé et de la Recherche Médicale (INSERM)-CHU Trousseau APHP; Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU)-Sorbonne Université (SU); Hôpital Cochin AP-HP |
| Source: |
European Respiratory Society ; https://inserm.hal.science/inserm-04213469 ; European Respiratory Society, Sep 2023, Milan (Italie), Italy |
| Publisher Information: |
CCSD |
| Publication Year: |
2023 |
| Subject Terms: |
Genetics; Quality of life; Treatments; [SDV.MHEP.PSR]Life Sciences [q-bio]/Human health and pathology/Pulmonology and respiratory tract; [SDV.GEN.GH]Life Sciences [q-bio]/Genetics/Human genetics |
| Subject Geographic: |
Milan (Italie); Italy |
| Description: |
International audience |
| Document Type: |
conference object; still image |
| Language: |
English |
| Availability: |
https://inserm.hal.science/inserm-04213469; https://inserm.hal.science/inserm-04213469v1/document; https://inserm.hal.science/inserm-04213469v1/file/MLeBrun.pdf |
| Rights: |
info:eu-repo/semantics/OpenAccess |
| Accession Number: |
edsbas.5A6C08DC |
| Database: |
BASE |