| Title: |
Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy |
| Authors: |
Mendell, Jerry R.; Al-Zaidy, Samiah A.; Lehman, Kelly J.; McColly, Markus; Lowes, Linda P.; Alfano, Lindsay N.; Reash, Natalie F.; Iammarino, Megan A.; Church, Kathleen R.; Kleyn, Aaron; Meriggioli, Matthew N.; Shell, Richard |
| Source: |
JAMA Neurology ; volume 78, issue 7, page 834 ; ISSN 2168-6149 |
| Publisher Information: |
American Medical Association (AMA) |
| Publication Year: |
2021 |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1001/jamaneurol.2021.1272 |
| Availability: |
https://doi.org/10.1001/jamaneurol.2021.1272; https://jamanetwork.com/journals/jamaneurology/articlepdf/2780250/jamaneurology_mendell_2021_oi_210023_1624467431.00495.pdf |
| Accession Number: |
edsbas.659D8730 |
| Database: |
BASE |