| Title: |
Time- and dose-dependent normalization of pathological lysosomal storage and biochemistry in the mucopolysaccharidosis ΙΙΙΒ (MPS ΙΙΙΒ, Sanfilippo syndrome type Β) mouse model by intracerebroventricular enzyme replacement therapy with ΒΜΝ 250, a ΝAGLU-ΙGF2 fusion pro |
| Authors: |
Aoyagi-Scharber, Mika; Vincelette, Jon; Lawrence, Roger; Crippen-Harmon, Danielle; Yip, Bryan K.; Baridon, Brian; Prill, Heather; Minto, Wesley C.; Van Vleet, Jeremy L.; Vitelli, Catherine; Adintori, Evan G.; Christianson, Terri; Tiger, Pascale M.N.; Lo, Melanie J.; Holtzinger, John; Chen, Eric; Webster, Katherine A.; Brown, Jillian R.; Fitzpatrick, Paul A.; LeBowitz, Jonathan H.; Bagri, Anil; Bullens, Sherry; Crawford, Brett E.; Bunting, Stuart |
| Source: |
Molecular Genetics and Metabolism ; volume 117, issue 2, page S21 ; ISSN 1096-7192 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2016 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/j.ymgme.2015.12.180 |
| Availability: |
http://dx.doi.org/10.1016/j.ymgme.2015.12.180; https://api.elsevier.com/content/article/PII:S1096719215003650?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S1096719215003650?httpAccept=text/plain |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ |
| Accession Number: |
edsbas.6A0EF6B7 |
| Database: |
BASE |