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Tranexamic acid versus placebo to prevent bleeding in patients with haematological malignancies and severe thrombocytopenia (TREATT): a randomised, double-blind, parallel, phase 3 superiority trial

Title: Tranexamic acid versus placebo to prevent bleeding in patients with haematological malignancies and severe thrombocytopenia (TREATT): a randomised, double-blind, parallel, phase 3 superiority trial
Authors: Estcourt, Lise J; McQuilten, Zoe K; Bardy, Peter; Cole-Sinclair, Merrole; Collins, Graham P.; Crispin, Philip J.; Curnow, Elinor; Curnow, Jennifer; Degelia, Amber; Dyer, Claire; Friebe, Adam; Floro, Lajos; Grand, Effie; Hudson, Cara; Jones, Gail; Joseph, Joanne; Kallmeyer, Charlotte; Karakantza, Marina; Kerr, Paul; Last, Sara; Lobo-Clarke, Maria; Lumley, Matthew; McMullin, Mary F; Medd, Patrick G.; Morton, Suzy M.; Mumford, Andrew D.; Mushkbar, Maria; Parsons, Joseph; Powter, Gillian; Sekhar, Mallika; Smith, Laura; Soutar, Richard; Stevenson, William S.; Subramoniapillai, Elango; Szer, Jeff; Thomas, Helen; Waters, Neil A.; Wei, Andrew H.; Westerman, David A.; Wexler, Sarah A.; Wood, Erica M.; Stanworth, Simon J.; Abioye, Adrienne; Afghan, Rabia; Ai, Sylvia Ai; Akanni, Magbor; Alajangi, Rajesh; Alam, Usmaan; Al-Bubseeree, Bahaa; Alderson, Sophie; Alderson, Craig; Ali, Sayed; Ali, Kabir; Alighan, Rookmeen; Allam, Rebecca Allam; Allen, Tania; Al-Sakkaf, Wesam; Ames, Kate; Anderson, Jacqueline; Andrews, Colin; Angel, Ann-Marie; Anlya, Manuela Anlya; Ansari, Farah; Appleby, Rowan; Arnold, Claire; Asbjornsdottir, Hulda; Asfaw, Biruk; Atkins, Elissa; Atkinson, Leela; Aubrey, Clare; Ayesha, Noor; Babbola, Lola; Badcock, David; Badcock, Samuel; Baggio, Diva; Bailiff, Ben; Baines, Kizzy; Baker, Holly; Baker, Victoria; Ball, Lindsay; Ball, Martin; Balquin, Irwin; Banks, Emma; Banos, George; Barnett, Jaytee; Barrie, Claire; Barron, Claire; Barton, Rebecca; Bason, Nina; Batta, Bindu; Bautista, Dianne; Bayley, Angela; Bayly, Emma; Baynes, Fionnuala; Bazargan, Ali; Bazeley, Rachel; Beadle, Yvonne; Beardsmore, Claire; Beattie, Kate; Bedford, Caroline; Behal, Rachna; Behan, Daniel; Bejan, Lilihna; Bell, Sarah; Bell, Karen; Bell, Louise; Bell, Kaitlyn; Benjamin, Reuben; Bennett, Sam; Benson, Gary; Benson, Warwick; Bent, Cameron; Bergin, Krystal; Berry, Alex; Besenyei, Stephanie; Besley, Caroline; Betteridge, Scott; Beveridge, Leigh; Bhattacharyya, Abir; Billen, Annelies; Bilmon, Ian; Binns, Emma; Birt, Mark; Bishop, David; Blanco, Andrea; Bleby, Lisa; Blemnerhet, Richard; Blombery, Piers; Blyth, Emily; Blythe, Nicola; Boal, Lauren; Boden, Ali; Bokhari, Syed W.I.; Bongetti, Elisa; Booth, Stephen; Borley, Jayne; Bowen, David; Bowers, Dawn; Boyd, Stephen; Bradley, Sarah; Bradman, Helen; Bretag, Peta; Brillante, Maria; Brockbank, Rachel; Brough, Yasmin; Brown, Ellen; Brown, Jo; Brown, Eleanor; Brown, Claire; Brown, Jenny; Brown, Susan; Browning, Joe; Brownsdon, Alex; Bruce, David; Brydon-Hill, Ruth; Buckwell, Andrea; Burgess, Dannielle; Burke, Glenda; Burley, Kate; Burney, Claire; Burns, David; Burrows, Samuel; burton, Kieran; Butler, Jason; Cambalova, Lenka; Camozzi, Maria C.; Campbell, Philip; Campfield, Karen; Campion, Victoria; Cargo, Catherine; Carmona, Julia; Carney, Dennis; Casan, Joshua; Cashman, Helen; Catt, Lorraine; Cattell, Michael; Cavill, Megan; Chadbone, Rachel; Chaganti, Sridhar; Chai, Yee; Chai, Khai Li; Chang, Joshua; Chapman, Judith; Chapman, Oliver G.; Chapter, Tamika; Charlton, Andrew; Chau, Celina; Chauhan, Saleena; Chavda, Nikesh; Chen, Frederick; Chen, Melody; Chen, Meng Xi; Chen, Melanie; Chen, Melissa; Cheok, Kathleen; Cheung, Mai; Chidgey, Luke; Chmielokliec, Karolina; Choi, Philip; Choi, Jae; Chok, Anne; Chopra, Ruchika; Christopherson, Louise; Chu, Vicky; Chua, Chong Chyn; Chudakou, Pavel; Chugh, Vidushi; Chung, Chi; Clark, Erin; Clarke, Peter; Clarke, Kathleen; Clay, Jennifer; Clayton, Laura; Clements, Mitch; Clemmens, Jonathan; Clifford, Ruth; Collett, Dave; Collins, Maia; Collyer, Emily; Connolly, Maureen; Cook, Mark; Coombs, Sarah; Coppell, Jason; Cornwell, Sophie; Corrigan, Claire; Coughlin, Elizabeth; Couling, Jennifer; Cousins, Tony; Cowan, Catriona; Cox, Christine; Cox, Catherine; Coyle, Luke; Craig, Emily; Creasey, Thomas; Croan, Laura; Croft, Jane; Crosbie, Nicola; Crowe, Josephine; Crowther, Helen; Crozier, Jane; Culleton, Naomi; Cullis, Jonathan; Cumming, Anita; Cummins, Michelle; Cunningham, Adam; Curley, Cameron; Curtis, Samantha; Cuthbert, Robert; Cuthill, Kirsty; Dahahayake, Dinusha A; Dang, Amy; Davies, Marc; Davies, Ceri; Dawson, Emily; Day, Tom; De Abrew, Kanchana; De Lavallade, Hugues; De Silva, Neelaskshi; Dean, Georgina; Deane, Christopher; Demosthenous, Lisa; Desai, Amisha; Desborough, Michael; Devanny, Ian; Dhanapal, Jay; Dhani, Sundip; Di Martino, Vicky; Dickens, Emmy; DiCorleto, Carmen; Dinnett, Louise; Dirisan, Divya; Dixon, Karen; Dixon, Kiri; Doal, Inderjit; Dobivh, J; Docanto, Maria; Doecke, Helve; Donaldson, David; Donaldson, Kylee; Donohoe, Carrie; Douglas, Ashley; Doung, Stephen; Downer, Susan; D'Rozario, James; Drummond, Malcolm; Drummond, Mark; Drummond, Samantha; Drysdale, Elizabeth; D'Souza, Ross; D'Souza, Eugene; Dunn, Alex; Dutton, David; Dyson, Martin; Ediriwicurena, Kushani; Edleston, Sharon; Edwards, Dawn; Edwards, Morgan; Edwards, Anita; Eise, Nicole; Ellis, Steven; Ellis, Hayley; Elmonley, Shareef; Enstone, Rosemarie; Eordogh, Agnes; Erb, Sharon; Evans, Shannon; Evans, Megan; Ewing, Joanne; Eyre, Toby; Facey, Adam; Fammy, Mina; Farman, Jon; Farnell, Rachel; Favero, Laura; Fay, Keith; Ferguson, Karen; Fernon, Laura; Filshie, Robin; Finnegan, Damian; Fisher, Lisa; Flanagan, Asia; Fleck, Emma; Fletcher, Simon; Flora, Harpreet; Flower, Catherine; Fodor, Ioana; Foley, Heather; Folland, Emma; Folorunso, Comfort; Forbes, Molly; Fordwor, Katrina; Foster, Polly; Fox, Vanessa; Fox, Thomas; Francis, Olesya; Fryearson, Louise; Fuery, Madonna; Fung, Jiin; Furtado, Michelle; Galloway-Browne, Leanne; Gamble, Louise; Gamgee, Jeanette; Ganapathy, Arundathi; Gardner, Hayley; Gardner, Clare; Gasmelsheed, Noha; Gately, Amy; Gaynor, Lynda; Gebreid, Alex; Geffens, Ruth; George, Rachel; Gertner, Aniko; Ghebeh, Manar; Ghirardini, Emanuela; Giddings, Melainie; Gillett, Sandra; Gillett, Karen; Giri, Pratyush; Glass, Chris; Glewis, Sarah; Gooding, Sarah; Gordon, Olivia; Gordon, Joanne; Gottlieb, David; Gowda, Koushik; Gower, Elysie; Gray, Nicola; Grayer, Jo; Greaves, Elaine; Greenaway, Sally Anne; Greenfield, Graeme; Greenwood, Matthew; Gregory, Gareth; Griffin, James; Griffith, Julia; Griffith, James; Griffiths, Lindsey; Grzegrzolka, Paulina; Gu, Yisu; Guest, Jo; Guinai, Rosanna; Gullapalli, Veena; Gunolr, A.; Guo, Lina; H, Wayne; Hagua, Sophia; Haile, Senait; Hall, Richard; Hamdollah-Zadeh, Maryam; Hanif, Zahra; Hanlon, Kathleen; Hann, Nicholas; Hanna, Ramez; Hannah, Guy; Hapuarachchi, Sameera; Hardman, Jacinta; Hardy, Alison; Harris, Anthony; Harris, Kylie; Harrison, Beth; Harrison, Simon; Harrison, Lea-Anne; Harrop, Sean; Harvey, Caroline; Hatcliffe, Faye; Hawking, Jo; Hawkins, Matthew; Hayden, Janet; Hayman, Michelle; Haynes, Elizabeth; Heaney, Nicholas; Hebbard, Andrew; Hempton, Jenny; Hendunneti, Sasanka; Henry, Maeve; Heywood, Jonathan; Hildyard, Catherine; Hill, Lydia; Hilldrith, Annette; Hitev, Petar; Hiwase, Smita; Hiwase, Devendra; Hoare, Chris; Hodge, Renate; Holloway, Amy; Holt, Chloe; Holton, Kelly; Homer, Lauren; Horne, Gillian; Horvath, Noemi; Hotong, Linda; Houdyk, Kristen; Houseman, Katy; Hoxhallari, Ilda; Hsu, Hannah; Hsu, Nina; Huang, Gillian; Hudson, Kerryn; Hufton, Melanie; Hughes, Timothy; Hughes, Siobhan; Hurley, Kate; Huxley, Rosie; Ibitoye, Temitope; Ibrouf, Abubaken; Inam, Farha; Indran, Tishya; Ingham, Karen; Innes, Calum; Irvine, David; Jaafar, Sarah; Jain, Manish; Jameson, Laura; Janjua, Pardeep; Jarvis, Rebecca; Jatheendran, Abirami; Javed, Abbie; Jen, Sheila; Jobanpura, Shailesh; Jobson, Irene; John, Deborah; Johns, Sophie; Johnston, Amanda; Jones, Hollie; Jones, Francesca; Joniak, Karolina; Jovanovic, Michael; Jovic, Anita; Joyce, Lauren; Judd, Andrew; Kakarlamudi, Sudhakar; Kakaroubas, Nick; Kalita, Maggie; Kam, Shirly; Kan, Julie; Kandle, P; Kanellopoulos, Alex; Kao, Chien; Kaparou, Maria; Kartsios, Charamlampos; Katsioulas, Vicki; Kaye, Russell; Keen, Katie; Kelly, Richard; Kelly, Pauline; Kelly, Donna; Kelly, Melanie; Kennedy, Glen; Kennedy, Nola; Kenny, Angela; Kenworthy, Zoe; Kerridge, Ian; Kesavan, Murali; Khafizi, Angelika; Khakwani, Muhammad; Khalid, Amna; Khamly, Kate; Khan, Anjum; Khan, Dalia; Khan, Mojid; Khan, Lubna; Khoo, Mona; Khwaja, Asim; Kim, Grace; King, Andrew; King, Vicky; King, Donna; Kinsella, Francesca; Kipp, David; Kirandeep, Pachoo; Kirui, Laura C.; Kishore, Bhuvan; Knectlhi, Christopher; Knot, Amy; Knot, Armit; Ko, Cathy; Kolaric, Caitlin; Koo, Ray; Kotadia, Mary; Kothari, Jaimal; Kottaridis, Panagiotis D.; Kuiluinathan, Gajan; Kulasekararaj, Austin; Kwan, John; Kwok, Marwan; Kwok, Phillip; Kwok, Fiona; Laane, Kristiina; Lad, Deena; Laird, Jennifer; Lam, Ada; Lane, Mary; Lanenco, Monica; Lang, Susan; Langridge, Alex; Langton, Catherine; Lannon, Michelle; Latif, Annie; Latimer, Maya; Latter, Ruth; Lau, I-Jun; Lawless, Sarah; Lawless, Theresa; Leach, Mike; Leaney, Sarah; Leary, Heather; Leavy, James; LeBlanc, Abbey; Lee, Vivienne; Lee, Edwin; Lee, Jenny; Lee, Tamara; Leischkie, Marian; Leitinger, Emma; Leon, Christopher; Leonard, Jayne; Lewis, David; Lewis, Ian; Lewis, Tania; Lim, Daniel; Littlewood, Kelly; Liu, Dara; Loh, Joanna; Lokare, Anand; Lomas, Oliver; Lovell, Richard; Lowe, Theresa; Lowry, Lisa; Lubowiecki, Marcin; Lumb, Rebecca; Lynch, Gail; Macaulay, Amanda; MacDonald, Lyndsey; MacDonald-Burn, Jill; Macmillan, Margaret; Maddock, Karen; Mahaliyana, Tomas; Mahon, Cassandra; Maidment, Alison; Maier, Susie; Mairos, Michelle; Majid, Mahseeman; Mak, Ka L; Mak, Anne; Malendrayogau, Arunthrthy; Malham, Hana; Malyon, Felicity; Mandadapu, Vineela; Mandel, Laura; Mant, Sarah; Manton, Ruth; Maouche, Nadjoua; Maqbool, Muhammad G.; Marchant, Gregory; Marinho, Mariana; Marks, David; Marner, Mike; Marr, Helen; Marshall, Gillian; Martin, Siobhan; Martin, Abigail; Marzolini, Maria; Mason, Kiara; Massie, Jonathan; Masson, Rebecca; Mathavan, Vidya; Mathew, Siju; Mathie, Judith; Mattocks, Lehenta; Maybury, Bernard; Mayer, Georgina; McAlister, Chyrelle; McAllister, Jo; McConnell, Stewart; McCracken, James; McCullagh, Liz; McCulloch, Rory; Mcdermott, Christopher; Mcdonald, Kerian; McGinniss, Laura; McGurk, Fiona; McIlwain, Jessica; McIver, Kirsten; McKay, Pam; McKenna, Lorraine; Mclornan, Donal; McMahon, Coalon; McNeice, Linda; McNeill, Susan; McNickle, Molly; McQueen, Fiona; McRae, Simon; McTaggart, Bobby; Mehew, Jenny; Mehra, Varnn; Melly, Michelle; Menichelli, Tara; Micklethwatte, Ken; Mihailescue, Loredana; Mijovic, Aleksander; Millband, Hannah; Miller, Lucy; Millien, Samuel T.; Milnthorpe, James; Minson, Adrian; Molnar, Eva; Monsour, Marc; Moody, Mary; Moon, Rebecca; Moore, Sally; Moore, Katy; Morgan, Kelly; Morralley, Rebecca; Morris, Denise; Morris, Kirk; Morrison, Nicole; Moss, Merinda; Mughal, Muhammad; Muir, Paul; Mukkath, David; Mulla, Aasiyu; Mulligan, Stephen; Mullings, Joanne; Mulqueen, Angela; Muluey, Caitlin; Murdoch, Sarah; Murrani, Sura; Murthy, Vidhya; Musngi, Jimmy; Mustafa, Nadreen; Mynes, Tracey; Nalpantidis, Anastasios; Nandurkar, Harshal; Nardone, Linda; Nasari, Latifa; Nash, Monica; Naylor, Georgina; Ngu, Loretta; Nguethina, Melissa; Nguyen, John; Nguyen, Joseph; Nichol, Wendy; Nicholls, Emma; Nicole, Catherine S.; Nicolson, Phillip; Nielson, David; Nikolousis, Emmanouil; Nix, Georgina; Njoku, Rita; Norman, Jane; Norman, Amy; Norris, Phoebe; North, Daniel; Norwood, Megan; Notcheva, Gaynor; Novitzky-Basso, Igor; Nyaboko, Joseph; Nygren, Maria; Obu, Ingrid; O'Connell, Siobhan; O'Connor, Jody; O'Kelly, Deanna; O'Niell, Aideen; Ony, Jeremy; Oo, Kathy; Oo, April; Oppermann, Anne; Orr, Ruth; O'Sullivan, Mary; Page, Jennifer; Palfreyman, Emma; Paneesha, Shankaranarayana; Panicker, Shyam; Parbutt, Catherine; Parigi, Elesha; Paris, Gemma; Parker, Tracey; Parnell, Caroline; Parrish, Christopher; Parsons, Alex; Pasat, Mioara; Patel, Natasha; Patel, Vijay; Patel, Pooja; Patel, Chaya; Pati, Nalini; Patterson, Andrea; Paul, Lauren; Payet, Danielle; Payne, Elspeth; Peachey, Victoria; Pearson, Amanda; Peniket, Andy; Percy, Laura; Pereyra, Millicent; Pervaiz, Omer; Phalod, Gunjan D; Pham, Anh; Pho, Jason; Pickard, Keir; Pidcock, Michael; Piggin, Anna; Pishyar, Yalda; Pocock, Abigail; Pol, Ranjendres; Polzella, Paolo; Poolan, Sonia; Portingale, Vicki; Posnett, Claire; Potluri, Sandeep; Potter, Victoria; Pratt, Guy; Prodger, Catherine; Pueblo, Andres; Puliyayil, Anish; Puvanakumar, Pratheepan; Qadri, Abdul; Quach, Hang; Quinn, Michael; Rafferty, Mark; Rahman, Marzia; Raj, Kavita; Raj, Sonia; Rajendran, Ramina; Ramanan, Radha; Ramasamy, Karthik; Rampotas, Alexandros; Ranchhod, Natasha; Rashid, Sabia; Ratanjee, Sunita; Rathore, Gurpreet; Ratnasingam, Sumita; Rayat, Manjit; Rayner, Michael; Reddell-Denton, Rebecca; Redding, Nicola; Reddy, Udaya; Rehman, Atique; Rice, Carol; Riches, Iwona; Rider, Thomas; Riley, John; Rinaldi, Ciro; Roberts, Kayleigh; Roberts, Andrew; Robertson, Bryony; Robertson, Peter; Robinson, Dan; Robinson, Rebecca; Robjohns, Emma; Robledo, Laura; Rodrigues, Ana; Rofe, Chris; Roff, Bridie; Rogers, Rachel; Rolt, Jill; Rooney, Carmela; Rose, Kathy; Rose, Hannah; Ross, David; Rouf, Shahara; Rourke, Claire; Routledge, David; Ruggiero, Janet; Rule, Simon; Rumsey, Richard; Sagge, Cherry; Saldhana, Helen; Salisbury, Richard; Salisbury, Sarah; Salvaris, Ross; Sanders, Kay; Sangombe, Mirriam; Sanigorska, Anna; Santos, Kristine; Sarkis, Taylah; Sarma, Anita; Saunders, Natalie; Schmidt, Kara; Schmidtmann, Anja; Schumacher, Ann; Scorer, Tom Scorer; Scott, Asleigh; Seath, Ingrid; Sejman, Frances; Selim, Adrian; Shamim, Nadia; Shan, Jocelyn; Shanmuganathan, Naranie; Shanmugaranjan, Shaminie; Sharpe, Michelle; Sharpley, Faye; Shaw, Emma; Sheath, Cara; Sheehy, Oonagh; Shen, Vivian; Sherbide, Solomon; Sheridan, Mathew; Sheridan, Jane; Sheridon, Matthew; Shields, Tracy; Sim, Hau V; Sim, Shirlene; Sims, Matt; Singaraveloo, Lydia; Singh, Gurcharan; Singh, Jasmine; Sladesal, Shree; Sloan, Andrew; Slobodian, Peter; Smith, Sophie; Smith, Sarit; Smith, Claire; Smith, Alastair; Smith, Neil; Snowden, Katherine; Solis, Joel; Somios, Denise; Soo, Jade; Spanevello, Michelle; Spaulding, Madeleie; Spence, Laura; Spillane, Liz; Spiteri, Alisha; Sprigg, Naomi; Springett, Sally; Stafford, Lynn; Stainthorp, Katherine; Stark, Kate; Steeden, Louise; Stephen, Ella; Stephenson, Aisling; Stewart, Andrew; Stewart, Orla; Stobie, Emma; Stokes, Chelsea; Streater, Jacqui; Suddens, Charlie-Marie; Suntharalingam, Surenthini; Surana, Narinder; Sutherland, Robyn; Sutherland, Antony; Sutton, David; Sweeney, Connor; Sweet, Reilly; Szucs, Aniko P; Taheri, Leila E.; Tailor, Hinesh; Tam, Constantine; Tambakis, George; Tamplin, Mary; Tan, Chee; Tan, Sui; Tan, Joanne; Tan, Zhi; Taran, Tatiana; Tarpey, Fiona; Taseka, Angela; Tasker, Suzy; Tatarczuch, Maciej; Tayabali, Sarrah; Taylor, Hannah; Taylor, Robert; Taylor, Melaine; Taylor-Moore, Ella; Teasdale, Lesley; Tebbet, Elizabeth; Tedjasepstra, Aditya; Tedjaseputra, Aditya; Tepkumkun, Oummy; Terpstra, Andrew; Thomas, Wayne; Thomas, Shanice; Thompson, Rachel; Thornton, Thomas; Thorp, Bronwyn; Thrift, Moi Yap; Thwaites, Phillipa; Timbres, Jasmine; Tindall, Lauren; Tiong, Ing Soo; Tippler, Nicole; Todd, Tony; Todd, Shirley; Toghill, Neil; Tomlinson, Eve; Tooth, Jacinta; Topp, M.; Trail, Nicola; Tran, Nguyen; Tran, Elizabeth; Tran, Vi; Treder, Bona; Tribbeck, Michelle; Trochowski, Siobhan; Truslove, Maria; Tse, Tsun; Tseu, Bing; Tucker, David; Turner, Kelly; Turner, Dianne; Turner, Herleen; Turner, Gillian; Twohig, Julie; Tylee, Thomas; Uhe, Micheleine; Underhill, Lauren; V, Joanne; Van der Vliet, Georgina; Van Tonder, Tina; VanderWeyden, Carrie; Varghese, Jerry; Vaughan, Lachlan; Veale, David; Vickaryyous, Nicky; Vince, Kathryn; Von Welligh, Jacoba; Vora, Sona; Wadehra, Karan; Walker, Rebecca; Walker, Stephen; Wallace, Roslyn; Wallniosve, Stephanie; Wallwork, S.; Walmsley, Zoe; Walters, Fiona; Wang, Joyce; Wang, Angela; Wang, Chen; Wanyika, Mercy; Warcel, Dana; Wardrobe, Katrina; Warnes, Kristian; Waterhouse, Christopher; Waterworth, Adam; Watson, Caroline; Watson, Edmund; Watts, Emily; Weaver, Emma; Weber, Nicholas; Webley, Kaytie; Welford, Anna; Wells, Matt; Westbury, Sarah; Westcott, Jackie; Western, Robyn; Weston, Julia; White, Jessica; White, Phillipa; Whitehead, Anna; Whitehouse, James; Wieringa, Samantha; Willan, John; Williams, Sandra; Williams, Bethany; Williamson, Stephanie; Willoughby, Brett; Wilmot, Gail; Wilmott, Rosalind; Wilson, Joanna; Wilson, Emma; Wilson, Suzy; Wilson, Heather; Wilson, Caroline; Wilson, Tanya; Wilton, Margaret; Wiltshire, Paula; Wincup, Joanne; Wolf, Julia; Wong, Henna; Wong, Cyndi; Wong, Daniel; Wong, Jonathan; Wong, Shi Qin; Wood, Sarah; Wood, Henry; Wooding, Jackie; Woolley, Kelly; Wright, Myles; Wynn-Williams, Roland; Yannakou, Costas; Yeoh, Zhi Han; Yeung, David; Young, Agnes; Yuen, Flora; Yuen, Agnes; Zaja, Oliver; Zhang, Xiao-Yin; Zhang, Mei
Publisher Information: Elsevier
Publication Year: 2025
Collection: University of Glasgow: Enlighten - Publications
Description: Background: Bleeding is common in patients with haematological malignancies undergoing intensive therapy. We aimed to assess the effect of tranexamic acid on preventing bleeding and the need for platelet transfusions. Methods: TREATT was an international, randomised, double-blind, parallel, phase 3 superiority trial conducted at 27 haematology centres in Australia and the UK. We enrolled adults (aged ≥18 years) receiving intensive chemotherapy or haematopoietic stem-cell transplantation for a haematological malignancy, with a platelet count of 10 × 109 platelets per L or less for 5 days or longer. Patients were randomly assigned (1:1) using block randomisation, stratified by site, to tranexamic acid (1 g every 8 h intravenously or 1·5g every 8 h orally) or placebo when their platelet count was less than 30 × 109 platelets per L. Treatment was continued until platelet recovery or day 30. Prophylactic platelet transfusions were maintained as standard of care. The primary endpoint was the proportion of patients who died or had WHO grade 2 or higher bleeding up to day 30. A modified intention-to-treat population including randomly assigned patients whose platelet count decreased to 30 × 109 platelets per L or less was used for analysis. This trial is registered with ClinicalTrials.gov (NCT03136445), ISRCTN (ISRCTN73545489), and the European Clinical Trials Register (EudraCT 2014-001513-35). Findings: Between June 23, 2015, and Feb 17, 2022, 1736 patients were screened for eligibility, 616 of whom were enrolled and randomly assigned (310 to tranexamic acid and 306 to placebo). 19 participants were excluded from the modified intention-to-treat analysis, leaving 300 participants in the tranexamic acid group and 297 in the placebo group. Participant median age was 58 years (IQR 49–65), 380 (62%) of 616 participants were male, and 235 (38%) were female. The proportion of participants who died or had WHO grade 2 or higher bleeding was 31·7% (90/298 [95% CI 26·6–37·4]) in the tranexamic acid group and 34·2% (98/295 ...
Document Type: article in journal/newspaper
Language: unknown
Relation: Estcourt, L. J. et al. (2025) Tranexamic acid versus placebo to prevent bleeding in patients with haematological malignancies and severe thrombocytopenia (TREATT): a randomised, double-blind, parallel, phase 3 superiority trial. Lancet Haematology , 12(1), e14-e22. (doi:10.1016/S2352-3026(24)00317-X ) (PMID:39642900)
Availability: https://eprints.gla.ac.uk/343277/
Accession Number: edsbas.7C3C3750
Database: BASE