| Title: |
OC 20.2 Gene Therapy in Hemophilia A: The Impact of Valoctocogene Roxaparvovec on Patient Outcomes – Initial Results from Patient Reported Outcomes, Burdens and Experiences (PROBE) from the GENEr8-1 Trial |
| Authors: |
Skinner, M.; Chen, E.; Ibrahim, Q.; Kucher, A.; Germini, F.; Karimi, M.; Clearfield, E.; O’Mahony, B.; Jain, M. |
| Source: |
Research and Practice in Thrombosis and Haemostasis ; volume 7, page 100429 ; ISSN 2475-0379 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2023 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/j.rpth.2023.100429 |
| Availability: |
http://dx.doi.org/10.1016/j.rpth.2023.100429; https://api.elsevier.com/content/article/PII:S2475037923040542?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S2475037923040542?httpAccept=text/plain |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ ; http://creativecommons.org/licenses/by-nc-nd/4.0/ |
| Accession Number: |
edsbas.94673FDB |
| Database: |
BASE |