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MYCOPHENOLATE MOFETIL TREATMENT REDUCES THE RISK OF TREATMENT ESCALATION DUE TO VASCULAR COMPLICATIONS IN LIMITED CUTANEOUS SYSTEMIC SCLEROSIS: EMULATION OF A TARGET TRIAL FROM ITALIAN RHEUMATOLOGY SOCIETY SPRING REGISTRY

Title: MYCOPHENOLATE MOFETIL TREATMENT REDUCES THE RISK OF TREATMENT ESCALATION DUE TO VASCULAR COMPLICATIONS IN LIMITED CUTANEOUS SYSTEMIC SCLEROSIS: EMULATION OF A TARGET TRIAL FROM ITALIAN RHEUMATOLOGY SOCIETY SPRING REGISTRY
Authors: Enrico De Lorenzis; Gerlando Natalello; Rossella De Angelis; Lucrezia Verardi; Dilia Giuggioli; Gianluigi Bajocchi; Lorenzo Dagna; Silvia Bellando-Randone; Giovanni Zanframundo; Rosario Foti; Fabio Cacciapaglia; Giovanna Cuomo; Alarico Ariani; Edoardo Rosato; Gemma Lepri; Francesco Girelli; Valeria Riccieri; Elisabetta Zanatta; Ilaria Cavazzana; Francesca Ingegnoli; Maria De Santis; Giuseppe Murdaca; Giuseppina Abignano; Giorgio Pettiti; Alessandra Della Rossa; Maurizio Caminiti; Annamaria Iuliano; Giovanni Ciano; Lorenzo Beretta; Gianluca Bagnato; Ennio Lubrano; Maria Ilenia De Andres; Alessandro Giollo; Cosimo Bruni; Martina Orlandi; Marco Fornaro; Marta Saracco; Cecilia Agnes; Pier Giacomo Cerasuolo; Gabriella Alonzi; Edoardo Cipolletta; Federica Lumetti; Amelia Spinella; Luca Magnani; Corrado Campochiaro; Giacomo De Luca; Veronica Codullo; Elisa Visalli; Carlo Iandoli Antonietta Gigante; Greta Pellegrino; Erika Pigatto; Maria-Grazia Lazzaroni; Franco Franceschini; Elena Generali; Gianna Mennillo; Simone Barsotti; Giuseppa Pagano Mariano; Federica Furini; Licia Vultaggio; Simone Parisi; Clara Lisa Peroni; Gerolamo Bianchi; Enrico Fusaro; Gian Domenico Sebastiani; Marcello Govoni; Salvatore D'Angelo; Franco Cozzi; Fabrizio Conti; Serena Guiducci; Andrea Doria; Carlo Salvarani; Florenzo Iannone; Maria Antonietta D’Agostino; Clodoveo Ferri; Marco Matucci Cerinic; Silvia Laura Bosello
Contributors: De Lorenzis, Enrico; Natalello, Gerlando; De Angelis, Rossella; Verardi, Lucrezia; Giuggioli, Dilia; Bajocchi, Gianluigi; Dagna, Lorenzo; Bellando-Randone, Silvia; Zanframundo, Giovanni; Foti, Rosario; Cacciapaglia, Fabio; Cuomo, Giovanna; Ariani, Alarico; Rosato, Edoardo; Lepri, Gemma; Girelli, Francesco; Riccieri, Valeria; Zanatta, Elisabetta; Cavazzana, Ilaria; Ingegnoli, Francesca; De Santis, Maria; Murdaca, Giuseppe; Abignano, Giuseppina; Pettiti, Giorgio; Della Rossa, Alessandra; Caminiti, Maurizio; Iuliano, Annamaria; Ciano, Giovanni; Beretta, Lorenzo; Bagnato, Gianluca; Lubrano, Ennio; Ilenia De Andres, Maria; Giollo, Alessandro; Bruni, Cosimo; Orlandi, Martina; Fornaro, Marco; Saracco, Marta; Agnes, Cecilia; Giacomo Cerasuolo, Pier; Alonzi, Gabriella; Cipolletta, Edoardo; Lumetti, Federica; Spinella, Amelia; Magnani, Luca; Campochiaro, Corrado; De Luca, Giacomo; Codullo, Veronica; Visalli, Elisa; Iandoli Antonietta Gigante, Carlo; Pellegrino, Greta; Pigatto, Erika; Lazzaroni, Maria-Grazia; Franceschini, Franco; Generali, Elena; Mennillo, Gianna; Barsotti, Simone; Pagano Mariano, Giuseppa; Furini, Federica; Vultaggio, Licia; Parisi, Simone; Lisa Peroni, Clara; Bianchi, Gerolamo; Fusaro, Enrico; Domenico Sebastiani, Gian; Govoni, Marcello; D'Angelo, Salvatore; Cozzi, Franco; Conti, Fabrizio; Guiducci, Serena; Doria, Andrea; Salvarani, Carlo; Iannone, Florenzo; Antonietta D’Agostino, Maria; Ferri, Clodoveo; Matucci Cerinic, Marco; Laura Bosello, Silvia
Publication Year: 2026
Collection: Archivio della ricerca dell'Università di Modena e Reggio Emilia (Unimore: IRIS)
Description: Objective Mycophenolate Mofetil (MMF) use in limited cutaneous systemic sclerosis (lcSSc) is relatively uncommon due to the lower fibrotic burden and the predominance of the vascular complications. In vitro observations and clinical data from transplanted patients suggest a protective effect of MMF on endothelial function. Our aim was to evaluate the reasons for prescribing MMF treatment in patients with lcSSc and its impact on the need for escalation of vascular complication–related treatments during follow-up. Methods LcSSc patients enrolled in the Italian SPRING registry were retrospectively evaluated. All patients treated with MMF were matched to patients not treated with MMF, based on a roll-entry time-dependent propensity score built on demographics, clinical features and baseline treatment. The escalation of vasoactive or vasodilator treatment up to 60 months was defined as the introduction of iloprost, endothelin receptor antagonists, or phosphodiesterase-5 inhibitors on top of the ongoing treatment, due to uncontrolled or newly diagnosed vascular complications. A hazards Cox model was also adopted to quantify the association of MMF treatment with treatment escalation. Results A total of 1,435 lcSSc patients were evaluated, of whom 152 were prescribed MMF (17.1% male; mean age at lcSSc onset 48.7±13.9 years, 54.6% anti-Scl70 positive). The prescription of MMF was more common in 21514658, ja, Downloaded from https://acrjournals.onlinelibrary.wiley.com/doi/10.1002/acr.70039 by Dilia Giuggioli - University Modena , Wiley Online Library on [16/01/2026]. See the Terms and Conditions (https://onlinelibrary.wiley.com/terms-and-conditions) on Wiley Online Library for rules of use; OA articles are governed by the applicable Creative Commons License Mycophenolate mofetil and vascular complications of systemic sclerosis males and in anti-Scl70 positive patients, anti-centromere negative, and in patients with interstitial lung disease, myositis, and without a history of digital ulcers. After matching 107 patients ...
Document Type: article in journal/newspaper
Language: English
Relation: firstpage:1; lastpage:20; journal:ARTHRITIS CARE & RESEARCH; https://hdl.handle.net/11380/1393756
DOI: 10.1002/acr.70039
Availability: https://hdl.handle.net/11380/1393756; https://doi.org/10.1002/acr.70039
Rights: info:eu-repo/semantics/openAccess ; license:[IR] publisher-specific-oa ; license uri:publisher
Accession Number: edsbas.99551BDC
Database: BASE