CRISPR-Cas9 correction of OPA1 c.1334G > A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs
| Title: | CRISPR-Cas9 correction of OPA1 c.1334G > A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs |
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| Authors: | Sladen, PE; Perdigao, PRL; Salsbury, G; Novoselova, T; van der Spuy, J; Chapple, JP; Yu-Wai-Man, P; Cheetham, ME |
| Publication Year: | 2021 |
| Collection: | Queen Mary University of London: Queen Mary Research Online (QMRO) |
| Document Type: | article in journal/newspaper |
| File Description: | 432 - 443 |
| Language: | unknown |
| Relation: | MOLECULAR THERAPY-NUCLEIC ACIDS; https://qmro.qmul.ac.uk/xmlui/handle/123456789/90555 |
| DOI: | 10.1016/j.omtn.2021.08.015 |
| Availability: | https://qmro.qmul.ac.uk/xmlui/handle/123456789/90555; https://doi.org/10.1016/j.omtn.2021.08.015 |
| Rights: | Attribution 3.0 United States ; http://creativecommons.org/licenses/by/3.0/us/ |
| Accession Number: | edsbas.B31D29FF |
| Database: | BASE |