| Title: |
480. Gene Therapy for Spinal Muscular Atrophy Type 1 Shows Potential to Improve Survival and Motor Functional Outcomes |
| Authors: |
Mendell, Jerry R.; Al-Zaidy, Samiah; Shell, Richard; Arnold, W Dave; Rodino-Klapac, Louise; Kissel, John T.; Prior, Thomas W.; Miranda, Carlos; Lowes, Linda; Alfano, Lindsay; Berry, Katherine; Petek, Christopher; Church, Kathleen; Braun, Lyndsey; Corcoran, Sarah; Meyer, Kathrin; Likhite, Shibi; Burghes, Arthur HM; Foust, Kevin D.; Kaspar, Brian K. |
| Source: |
Molecular Therapy ; volume 24, page S190 ; ISSN 1525-0016 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2016 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/s1525-0016(16)33289-0 |
| Availability: |
http://dx.doi.org/10.1016/s1525-0016(16)33289-0; https://api.elsevier.com/content/article/PII:S1525001616332890?httpAccept=text/plain; https://api.elsevier.com/content/article/PII:S1525001616332890?httpAccept=text/xml |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ ; http://creativecommons.org/licenses/by-nc-nd/4.0/ |
| Accession Number: |
edsbas.DDB8E119 |
| Database: |
BASE |