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Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial

Title: Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial
Authors: Machado, Pedro M; McDermott, Michael P; Blaettler, Thomas; Sundgreen, Claus; Amato, Anthony A; Ciafaloni, Emma; Freimer, Miriam; Gibson, Summer B; Jones, Sarah M; Levine, Todd D; Lloyd, Thomas E; Mozaffar, Tahseen; Shaibani, Aziz I; Wicklund, Matthew; Rosholm, Anders; Carstensen, Tim Dehli; Bonefeld, Karen; Jørgensen, Anders Nørkær; Phonekeo, Karina; Heim, Andrew J; Herbelin, Laura; Barohn, Richard J; Hanna, Michael G; Dimachkie, Mazen M; Dimachkie, Mazen; Statland, Jeffrey; Pasnoor, Mamatha; Jawdat, Omar; Heim, Andrew; Ciersdorff, Ali; Sasidharan, Sandhya; Currence, Melissa; Levine, Todd; Otutoa, Rebecca; Cooper, Angelina; Habib, Ali; Cauchi, Jonathan; Ung, Shannon; Mathew, Veena; Hernandez, Isela; Gibson, Summer; Bromberg, Mark; Mahoney, Kyle; Neate, Crystal; Janecki, Teresa; Papadakis, Mike; Kaschalk, MacKenzie; Heintzman, Sarah
Source: The Lancet Neurology ; volume 22, issue 10, page 900-911 ; ISSN 1474-4422
Publisher Information: Elsevier BV
Publication Year: 2023
Collection: ScienceDirect (Elsevier - Open Access Articles via Crossref)
Document Type: article in journal/newspaper
Language: English
DOI: 10.1016/s1474-4422(23)00275-2
Availability: http://dx.doi.org/10.1016/s1474-4422(23)00275-2; https://api.elsevier.com/content/article/PII:S1474442223002752?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S1474442223002752?httpAccept=text/plain
Rights: https://www.elsevier.com/tdm/userlicense/1.0/ ; http://creativecommons.org/licenses/by/4.0/
Accession Number: edsbas.EDB1684D
Database: BASE