| Title: |
Histologic characterization of the progression of central nervous system pathology in the mucopolysaccharidosis IIIB (MPS IIIB, Sanfilippo syndrome type B) mouse model and bio-distribution and efficacy of the intracerebroventricular enzyme replacement therapy, BMN 250 |
| Authors: |
Bagri, Anil; Harmon, Danielle; Vincelette, Jon; Vitelli, Catherine; Minto, Wesley; Yates, Bridget; Rigney, Sara; Santiago, Pam; Baridon, Brian; Xie, Lin; Gorostiza, Olivia; Christianson, Terri; Tiger, Pascale M.N.; Yip, Bryan K.; Lo, Melanie J.; Holtzinger, John; Chen, Eric; Aoyagi-Scharber, Mika; Fitzpatrick, Paul; LeBowitz, Jonathan H.; Bullens, Sherry; Bunting, Stuart |
| Source: |
Molecular Genetics and Metabolism ; volume 117, issue 2, page S23-S24 ; ISSN 1096-7192 |
| Publisher Information: |
Elsevier BV |
| Publication Year: |
2016 |
| Collection: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Document Type: |
article in journal/newspaper |
| Language: |
English |
| DOI: |
10.1016/j.ymgme.2015.12.187 |
| Availability: |
http://dx.doi.org/10.1016/j.ymgme.2015.12.187; https://api.elsevier.com/content/article/PII:S1096719215003728?httpAccept=text/xml; https://api.elsevier.com/content/article/PII:S1096719215003728?httpAccept=text/plain |
| Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ |
| Accession Number: |
edsbas.F46A6314 |
| Database: |
BASE |