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Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency

Title: Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency
Authors: Migliavacca, MaddalenaAff1, Aff2; Barzaghi, FedericaAff1, Aff2; Fossati, ClaudiaAff1; Rancoita, Paola M. V.Aff3; Gabaldo, MichelaAff4; Dionisio, FrancescaAff1; Giannelli, StefaniaAff1; Salerio, Federica AndreaAff1; Ferrua, FrancescaAff1, Aff2; Tucci, FrancescaAff1, Aff2; Calbi, ValeriaAff1, Aff2; Gallo, VeraAff1, Aff2; Recupero, SalvatoreAff1, Aff2; Consiglieri, GiuliaAff1, Aff2; Pajno, RobertaAff1, Aff2; Sambuco, MariaAff1, Aff2; Priolo, AlessioAff1, Aff2; Ferri, ChiaraAff5; Garella, VittoriaAff5; Monti, IlariaAff1; Silvani, PaoloAff6; Darin, SilviaAff1; Casiraghi, MiriamAff1; Corti, AmbraAff1; Zancan, StefanoAff4; Levi, MargheritaAff4; Cesana, DanielaAff1; Carlucci, FilippoAff7; Pituch-Noworolska, AnnaAff8; AbdElaziz, DaliaAff9; Baumann, UlrichAff10; Finocchi, AndreaAff11, Aff12; Cancrini, CaterinaAff11, Aff12; Ladogana, SaverioAff13; Meinhardt, AndreaAff14; Meyts, IsabelleAff15; Montin, DavideAff16, Aff17; Notarangelo, Lucia DoraAff18; Porta, FulvioAff19; Pasquet, MarlèneAff20; Speckmann, CarstenAff21, Aff22; Stepensky, PolinaAff23; Tommasini, AlbertoAff24; Rabusin, MarcoAff24; Karakas, ZeynepAff25; Galicchio, MiguelAff26; Leonardi, LuciaAff27; Duse, MarziaAff27; Guner, Sukru NailAff28; Di Serio, CleliaAff3, Aff29; Ciceri, FabioAff1, Aff5, Aff30; Bernardo, Maria EsterAff1, Aff2, Aff5; Aiuti, AlessandroAff1, Aff2, Aff5, IDs41591023027894_cor53; Cicalese, Maria PiaAff1, Aff2, Aff5
Source: Nature Medicine. 30(2):488-497
Database: Springer Nature Journals