| Title: |
Medical expenses and care pathways of patients with Pompe receiving myozyme: an observational study based on the French national healthcare database |
| Authors: |
Le Bras, AliciaAff1, IDs13023025038662_cor1; De Lonlay, PascaleAff2; Attarian, ShahramAff3; Brassier, AnaïsAff4; Durand-Zaleski, IsabelleAff1, Aff5, Aff6; Laforêt, PascalAff7; Arrassi, Azzeddine; Bedat-Millet, Anne-Laure; Béhin, Anthony; Beltran, Stéphane; Bouibede, Françoise Bouhour Fatima; Caillaud, Catherine; Chabrol, Brigitte; Champeaux, Murielle; Cintas, Pascal; Davion, Jean-Baptiste; Diab, Eva; Deibener-Kaminsky, Joelle; Demurger, Florence; Espil, Caroline; Esselin, Florence; Feillet, François; Fournier, Maxime; Froissart, Roseline; Ghorab, Karima; Gillet, Charlene; Gorce, Magali; Hamroun, Dalil; Hogrel, Jean-Yves; Huet, Frédéric; Krim, Elsa; Labarthe, François; Lagrange, Emmeline; Lebeau, Françoise; Lefeuvre, Claire; Magot, Armelle; Magy, Laurent; Maillet-Vioud, Marcel; Masingue, Marion; Mention, Karine; Michaud, Maud; Nadaj-Pakleza, Aleksandra; Nollet, Sylvain; Not, Adeline; Noury, Jean-Baptiste; Orlikowski, David; Paricio, Caroline; Perez, Thierry; Pichard, Samia; Prigent, Hélène; Renard, Dimitri; Ropars, Juliette; Sacconi, Sabrina; Salort-Campana, Emmanuelle; Sole, Guilhem; Spinazzi, Marco; Taithe, Frédéric; Taouagh, Nadjib; Tard, Céline; Tardieu, Marine; Toquet, Ségolène; Touati, Guy; Vandeputte, Patrick; Verschueren, Annie; Vincent, Didier; Walther-Louvier, Ulrike; Ziri, Taissir |
| Source: |
Orphanet Journal of Rare Diseases. 20(1) |
| Database: |
Springer Nature Journals |