Allele‐specific silencing therapy for Dynamin 2‐related dominant centronuclear myopathy
| Title: | Allele‐specific silencing therapy for Dynamin 2‐related dominant centronuclear myopathy |
|---|---|
| Authors: | Trochet, DelphineAff1; Prudhon, BernardAff1; Beuvin, MaudAff1; Peccate, CécileAff1; Lorain, StéphanieAff1; Julien, LauraAff1; Benkhelifa‐Ziyyat, SofiaAff1; Rabai, AymenAff2; Mamchaoui, KamelAff1; Ferry, ArnaudAff1; Laporte, JocelynAff2; Guicheney, PascaleAff3; Vassilopoulos, StéphaneAff1; Bitoun, MarcAff1, IDEMMM201707988_cor1 |
| Source: | EMBO Molecular Medicine. 10(2):239-253 |
| Database: | Springer Nature Journals |