Restoration of RPGR expression in vivo using CRISPR/Cas9 gene editing
| Title: | Restoration of RPGR expression in vivo using CRISPR/Cas9 gene editing |
|---|---|
| Authors: | Gumerson, Jessica D.Aff1, IDs41434021002586_cor1; Alsufyani, AmalAff1, Aff2, Aff3; Yu, WenhanAff4; Lei, JingqiAff5; Sun, XunAff1; Dong, LijinAff5; Wu, ZhijianAff4; Li, TiansenAff1, IDs41434021002586_cor8 |
| Source: | Gene Therapy. 29(12):81-93 |
| Database: | Springer Nature Journals |