AAV mini-dystrophin gene therapy for Duchenne muscular dystrophy: a phase 1b trial
| Title: | AAV mini-dystrophin gene therapy for Duchenne muscular dystrophy: a phase 1b trial |
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| Authors: | Butterfield, Russell J.Aff1; Shieh, Perry B.Aff2, IDs41591025037503_cor1; Li, HuihuaAff3; Binks, MichaelAff3; McDonnell, Tara G.Aff3; Ryan, Kelly A.Aff3; Delnomdedieu, MarielleAff3; Belluscio, Beth A.Aff3; Neelakantan, SrividyaAff3; Levy, Daniel I.Aff3; Schwartz, Pamela F.Aff3; Smith, Edward C.Aff4 |
| Source: | Nature Medicine. 31(8):2712-2721 |
| Database: | Springer Nature Journals |